Mucopolysaccharidosis type ⅢB:a current review and exploration of the AAV therapy landscape

Courtney J.Rouse; Victoria N.Jensen; Coy D.Heldermon

doi:10.4103/1673-5374.377606

🤖This page has been translated by AI and may contain inaccuracies. Please refer to the original content for clarification.

Home>Articles>Mucopolysaccharidosis type ⅢB:a current review and exploration of the AAV therapy landscape

DOI: 10.4103/1673-5374.377606

Mucopolysaccharidosis type ⅢB:a current review and exploration of the AAV therapy landscape

Courtney J.Rouse

Victoria N.Jensen

Coy D.Heldermon

Keywords：adeno-associated viruscentral nervous systemgene therapyheparan sulfateimmune responsemucopolysaccharidoses type ⅢBN-acetyl-alpha-glucosaminidasenewborn screening

Publication Date：2024-02-28

Online Publishing Date：2025-08-15(First online date of this platform, not the publication date of the document)

Pages：5( 355-359 )

Neural Regeneration Research

ISSN：1673-5374

Year, Vol.(Issue)：2024,19(2)